News and Trends 30 Oct 2019
Trial Testing Spinal Application of Zolgensma Put on Hold by FDA
The FDA has placed a partial hold on clinical trials testing a new application method for Zolgensma, Novartis’ gene therapy for the genetic disease spinal muscular atrophy, after it showed the potential to cause serious side effects in animal models. Spinal muscular atrophy is a life-threatening condition that usually arises when the patient is between […]