Gene therapy Archives

News and Trends 16 Aug 2022

Remedium raises more funds for osteoarthritis gene therapy candidate

Remedium Bio, Inc., a biotech company developing novel gene therapies, has closed more than $2.3 million in its expanded seed round financing. Funding from the raise is being used to study Remedium’s lead product, a single-injection gene therapy potentially capable of reversing cartilage loss. The study is being undertaken in a collaboration with Tufts University […]

August 16, 2022 - 3 minutesmins - By Jim Cornall

News and Trends 8 Aug 2022

Allogenic immune cell therapies to be developed as three groups join forces

Three entities have joined forces to develop allogenic immune cell therapies based on a platform that generates functionally mature immune cells from induced pluripotent stem cells (iPSCs). ElevateBio LLC is a technology-driven company focused on powering transformative cell and gene therapies. It announced recently (August 5) that it has formed a yet-to-be-named company co-founded by […]

August 8, 2022 - 3 minutesmins - By Liza Laws

News and Trends 4 Aug 2022

RoslinCT and Lykan Bioscience combine to create cell therapy CDMO

RoslinCT, a cell and gene therapy contract development and manufacturing organization (CDMO) developing life-changing therapies in Edinburgh’s BioQuarter, and Lykan Bioscience, a CDMO focused on cell-based therapies, have entered into a business combination agreement to form a global advanced therapies CDMO. The combined group will offer process development expertise and cGMP manufacturing for a range […]

August 4, 2022 - 2 minutesmins - By Jim Cornall

News and Trends 29 Jul 2022

Sarepta looks for quick approval for Duchenne muscular dystrophy gene therapy treatment

U.S. company Sarepta Therapeutics, Inc. said it intends to submit a Biologics License Application (BLA) seeking accelerated approval for SRP-9001 (delandistrogene moxeparvovec) to treat ambulant individuals with Duchenne muscular dystrophy. SRP-9001 is an investigational gene therapy for Duchenne being developed in partnership with Roche. “We are delighted to confirm that based on the feedback we […]

July 29, 2022 - 3 minutesmins - By Jim Cornall

News and Trends 29 Jul 2022

Commercial personalized cancer cell profile developed in Taiwan

Patients with stage 2 solid tumors could benefit from the world’s first commercial personalized cancer cell profiling, developed in Taiwan. Taipei-based CancerFree Biotech Ltd has developed the technology that will help stage 2 patients and above by shortening the selection process. The technology will be showcasing at US Bio 2022. This is the world’s first […]

July 29, 2022 - 3 minutesmins - By Liza Laws

News and Trends 28 Jul 2022

AGC Biologics announces gene therapy partnership with Altheia Science

A new development partnership between gene therapy company Altheia Sciences, which pioneers cell and gene treatments, and AGC Biologics, will look at strategies to treat autoimmune disease and cancer. Specifically, the partnership will help advance development of autoimmunity treatments, focused on modulating PD-L1 expression in patients’ hematopoietic stem and progenitor cells, into clinical testing. PD-L1 […]

July 28, 2022 - 2 minutesmins - By Liza Laws

News and Trends 27 Jul 2022

SomaLogic acquires DNA nanotechnology company Palamedrix

Colorado-based AI data-driven proteomics technology company SomaLogic has entered into an agreement to acquire Palamedrix, Inc., which is involved in DNA nanotechnology. Palamedrix provides scientific and engineering expertise and miniaturization technology, which SomaLogic intends to leverage as it develops the next generation of the SomaScan assay. Proteomic tool The SomaScan assay is a multiplexed, sensitive, quantitative, […]

July 27, 2022 - 3 minutesmins - By Liza Laws

News and Trends 26 Jul 2022

Oxford Biomedica sets up new project and signs LSA

Oxford Biomedica plc, a UK-based gene and cell therapy group, has initiated a new project with Orchard Therapeutics utilizing the company’s LentiStable technology. The group also announced the signing of a new licence and supply agreement (LSA) with an undisclosed US-based private biotech company advancing a new generation of adoptive cell therapies. LentiStable technology As […]

July 26, 2022 - 4 minutesmins - By Jim Cornall

News and Trends 20 Jul 2022

Upstaza gets nod from Europe for AADC deficiency treatment

PTC Therapeutics, Inc. says Upstaza (eladocagene exuparvovec) has been given marketing authorization by the European Commission. Upstaza is the first approved disease-modifying treatment for aromatic L-amino acid decarboxylase (AADC) deficiency, and the first marketed gene therapy directly infused into the brain. It is approved for patients 18 months and older. “Today’s approval from the European […]

July 20, 2022 - 3 minutesmins - By Jim Cornall

More News! 18 Jul 2022

Purespring Therapeutics and SwanBio Therapeutics announce agreement for use of FunSel screening platform

A licensing agreement for use of the FunSel screening platform has been announced by Purespring Therapeutics and SwanBio. Under the terms of the agreement, SwanBio will license the FunSel screening platform from Purespring to explore new targets for early-stage pipeline programs. SwanBio will have the option to develop any targets identified and to own and […]

July 18, 2022 - 2 minutesmins - By Liza Laws

News and Trends 5 Jul 2022

EditForce and Mitsubishi Tanabi Pharma to work on gene therapy for CNS

EditForce, Inc. has entered into a license agreement with Mitsubishi Tanabe Pharma Corporation (MTPC) to research, develop and commercialize potential gene therapy products for a specific target disease related to the central nervous system (CNS) by utilizing EditForce’s pentatricopeptide repeat (PPR) protein platform technology. MTPC and EditForce aim to create potential novel pharmaceuticals for the […]

July 5, 2022 - 2 minutesmins - By Jim Cornall

News and Trends 27 Jun 2022

Trial for adults with late onset Pompe disease halted due to serious adverse event

The US Food and Drug Administration (FDA) has placed a clinical hold on a trial being run for Astrellas Pharma Inc after one of the participants had a serious adverse event (SAE) of peripheral sensory neuropathy. Astrellas made the announcement after the trial, which is evaluating AT845, an investigational adeno-associated virus (AAV) gene replacement in […]

June 27, 2022 - 3 minutesmins - By Liza Laws

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Gene therapy

Remedium raises more funds for osteoarthritis gene therapy candidate

Allogenic immune cell therapies to be developed as three groups join forces

RoslinCT and Lykan Bioscience combine to create cell therapy CDMO

Sarepta looks for quick approval for Duchenne muscular dystrophy gene therapy treatment

Commercial personalized cancer cell profile developed in Taiwan

AGC Biologics announces gene therapy partnership with Altheia Science

SomaLogic acquires DNA nanotechnology company Palamedrix

Oxford Biomedica sets up new project and signs LSA

Upstaza gets nod from Europe for AADC deficiency treatment

Purespring Therapeutics and SwanBio Therapeutics announce agreement for use of FunSel screening platform

EditForce and Mitsubishi Tanabi Pharma to work on gene therapy for CNS

Trial for adults with late onset Pompe disease halted due to serious adverse event

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Catalonia: A biotech hub going from strength to strength, with Barcelona at its core

Top biotech deals of February 2025

Grab your free report on 3D organoids and explore their future potential

These 7 biotechs are shaping the next generation of endometriosis care

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

Catalonia: A biotech hub going from strength to strength, with Barcelona at its core

Top biotech deals of February 2025

Grab your free report on 3D organoids and explore their future potential

These 7 biotechs are shaping the next generation of endometriosis care

Connect with decision-makers and researchers worldwide for collaborative opportunities

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Advertise with us

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